Clinical reference
CFTR Modulator · Cystic fibrosis transmembrane conductance regulator (CFTR) potentiator · Pulmonology, Pediatrics, Cystic Fibrosis
Ivacaftor is a CFTR potentiator indicated for cystic fibrosis in patients with specific CFTR mutations (class 3; originally G551D; see product information for full list of approved mutations). Formulations: oral granules 25 mg, 50 mg, 75 mg (56 packets each); tablets 150 mg (56 tabs). Use granules for 4 to <6 months and for children <6 years; use tablets…